Completed


  • Engaging Duchenne Community

    Study Chair: R. Bendixen , L. Morgenroth ,
    Sponsor: Foundation to Eradicate Duchenne (FED)
    Publications: Clinical Therapeutics (2016) 6:1474-1486 ,
    Total Enrollment: 59
  • Duchenne Muscular Dystrophy Tissue Bank for Exon Skipping

    Study Chair: A. Harper
    Sponsor: National Institute of Health
    Publications: For access to tissue bank: info@cinrgresearch.org
    Total Enrollment: 53
  • Evaluation of LGMD

    Study Chair: S. Sparks
    Sponsor: Muscular Dystrophy Association
    Publications: Manuscript in draft
    Total Enrollment: 52
  • CNMC0609 Comparative Study of Clinical Endpoint: HHM vs. CQMS

    Study Chair: T. Duong
    Sponsor: Muscular Dystrophy Association
    Publications: Manuscript in draft
    Total Enrollment: 33
  • PITT1109 Cardiac Outcome Measures in Children with Muscular Dystrophy

    Study Chair: P. Clemens
    Sponsor: National Institute of Health
    Publications: JASE (2015) 28(8): 999-1008
    Total Enrollment: 48
  • CNMC0705 A Double-Blind Randomized Placebo-Controlled Study of Daily Pentoxifylline as Rescue Treatment in DMD

    Study Chair: D. Escolar
    Sponsor: Foundation to Eradicate Duchenne (FED)
    Publications: Neurology (2012) 78:904-913
    Total Enrollment: 64
  • CNMC0601 A Randomized Study of Daily vs. High Dose Weekly Prednisone in DMD

    Study Chair: D. Escolar , P. Clemens
    Sponsor: Muscular Dystrophy Association
    Publications: Neurology (2011) 77:444-452
    Total Enrollment: 64
  • CNMC0302 An Open-Label Pilot Study of Pentoxifylline in Steroid-Naïve DMD

    Study Chair: D. Escolar
    Sponsor: Muscular Dystrophy Association
    Publications: Muscle and Nerve (2011) 44:170-173
    Total Enrollment: 17
  • CNMC0599 A Multicenter Randomized Placebo-Controlled Double-Blind Study to Assess the Efficacy and Safety of Glutamine and Creatine in DMD

    Study Chair: D. Escolar
    Sponsor: Muscular Dystrophy Association
    Publications: Annals of Neurology (2005) 58:151–155
    Total Enrollment: 50
  • CNMC0301 An Open-Label Pilot Study of Coenzyme Q10 in Steroid-Treated DMD

    Study Chair: D. Escolar
    Sponsor: Muscular Dystrophy Association
    Publications: Muscle and Nerve (2011) 44:174-178
    Total Enrollment: 16
  • KUL0401 An Open-Label Pilot Study of Oxatomide in Steroid-Naive DMD

    Study Chair: G. Buyse , D. Escolar
    Sponsors: Association Française Contre les Myopathie, Muscular Dystrophy Association
    Publications: European Journal of Pediatric Neurology (2007) 11:337 – 340
    Total Enrollment: 14
  • CINRG Reliability Studies

    Study Chair: D. Escolar , J. Mayhew
    Publications: Muscle and Nerve (2001) 24:787-93 and , Muscle and Nerve (2007) 35:36-42
    Total Enrollment: 31