Completed


Study TitleStudy ChairSponsorPublicationsTotal Enrollment
CINRG Reliability StudiesD. Escolar
J. Mayhew
 

Muscle and Nerve (2001) 24:787-93   and Muscle and Nerve (2007) 35:36-42



31
KUL0401 An Open-Label Pilot Study of Oxatomide in Steroid-Naive DMDG. Buyse
D. Escolar
Association Française Contre les Myopathie

Muscular Dystrophy Association

European Journal of Pediatric Neurology (2007) 11:337 – 340



14
CNMC0301 An Open-Label Pilot Study of Coenzyme Q10 in Steroid-Treated DMDD. EscolarMuscular Dystrophy Association

Muscle and Nerve (2011) 44:174-178



16
CNMC0599 A Multicenter Randomized Placebo-Controlled Double-Blind Study to Assess the Efficacy and Safety of Glutamine and Creatine in DMDD. EscolarMuscular Dystrophy Association

Annals of Neurology (2005) 58:151–155



50
CNMC0302 An Open-Label Pilot Study of Pentoxifylline in Steroid-Naïve DMDD. EscolarMuscular Dystrophy Association

Muscle and Nerve (2011) 44:170-173



17
CNMC0601 A Randomized Study of Daily vs. High Dose Weekly Prednisone in DMDD. Escolar
P. Clemens
Muscular Dystrophy Association

Neurology (2011) 77:444-452



64
CNMC0705 A Double-Blind Randomized Placebo-Controlled Study of Daily Pentoxifylline as Rescue Treatment in DMDD. EscolarFoundation to Eradicate Duchenne (FED)

Neurology (2012) 78:904-913



64
PITT1109 Cardiac Outcome Measures in Children with Muscular DystrophyP. ClemensNational Institute of Health

JASE (2015) 28(8): 999-1008



48
CNMC0609 Comparative Study of Clinical Endpoint: HHM vs. CQMST. DuongMuscular Dystrophy Association

Manuscript in draft



33
Evaluation of LGMDS. SparksMuscular Dystrophy Association

Manuscript in draft



52
Duchenne Muscular Dystrophy Tissue Bank for Exon SkippingA. HarperNational Institute of Health

For access to tissue bank: info@trinds.com



53
Engaging Duchenne CommunityR. Bendixen
L. Morgenroth
Foundation to Eradicate Duchenne (FED)

Clinical Therapeutics (2016) 6:1474-1486



59
Clinical Features, Expression Profiling, and Quality of Life of Infantile Onset Facioscapulohumeral Muscular DystrophyJ. MahUnited States FSHD Society

FSHD Global Research Foundation

Muscular Dystrophy Canada

aTyr Pharma

Manuscript in Draft



53